Resources » Page 21

Gene Therapy: Past, Present, and Future

The second activity in the Clinical Advances in Gene Therapy for Hemophilia CME curriculum, Gene Therapy: Past, Present, and Future, is a round table video discussion of the evolution of gene therapy in hemophilia. Watch three experts reflect on the development, ongoing research, and current and future uses of gene therapy in hemophilia. A transcript […]

Test Your Knowledge of Gene Therapy in Hemophilia

The first activity in the Clinical Advances in Gene Therapy for Hemophilia CME curriculum, Test Your Knowledge of Gene Therapy in Hemophilia, is an educational self-assessment survey. The questions allow you to see how much you already know about gene therapy in hemophilia and the answers explain the essential information required for a fuller understanding. […]

Guide for the Assessment of Clotting Factor Concentrates

The purpose of this guide is to inform and facilitate the selection and purchase of therapeutic products for the treatment of hemophilia. It discusses the factors that contribute to the quality, safety, and efficacy of hemophilia treatment products and, in particular, the provisions made for ensuring that these products are free of viruses. It covers […]

Diagnosis of von Willebrand Disease: Phenotypic Characterization

The accurate diagnosis of von Willebrand disease (VWD) is crucial to its management. This resource describes laboratory tests based on the observable traits, or phenotype, of a person with bleeding symptoms and a positive family bleeding history that can be used to determine the specific type and variant of VWD. The companion monograph, TOH 56 […]

Report on the Annual Global Survey 2016

Compiled annually, the Annual Global Survey (AGS) provides demographic and other data on people with hemophilia, von Willebrand disease, other rare factor deficiencies, and inherited platelet disorders throughout the world.

Molecular Diagnosis of von Willebrand Disease

The accurate diagnosis of von Willebrand disease (VWD) is crucial to its management. This resource describes the techniques used to determine the genetic nature, or genotype, of a suspected case of VWD. The companion monograph, TOH 55 Diagnosis of von Willebrand Disease: Phenotypic Characterization, provides a detailed review of the laboratory tests that can be […]

Introduction to Bleeding Disorders

Adapted from: Global NMO Training 2016 plenary presentation by Glenn PierceReviewed by: Glenn PierceEdited by: Georghia Michael This first eLearning module of the Treatment Products program explains how blood clots, how  clotting factors work together in the coagulation cascade, what goes wrong in the case of factor deficiency, and how factor replacement therapy works by […]

Annual Global Survey Mini Report 1: Gender

The WFH Annual Global Survey (AGS) mini reports are advocacy tools that provide more in-depth perspective and context to AGS data. Lack of diagnosis and treatment for women and girls with bleeding disorders remains a challenge in our community. Highlighting gender data from the AGS can help bring awareness to the issues facing women and […]