Gene therapy

WFH Gene Therapy Registry – User guide for hemophilia treatment centres – Italian

The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved in gene therapy. This includes HTCs that administer gene therapy and those that manage or follow-up with patients who have received gene therapy at other centres. This user guide will orient HTCs to the WFH […]

WFH Gene Therapy Registry – User guide for hemophilia treatment centres – German

The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved in gene therapy. This includes HTCs that administer gene therapy and those that manage or follow-up with patients who have received gene therapy at other centres. This user guide will orient HTCs to the WFH […]

What is gene therapy?

This patient handbook contains basic information about gene therapy for hemophilia. The WFH does not engage in the practice of medicine and under no circumstances recommends particular treatment for specific individuals. For diagnosis or consultation on a specific medical problem, the WFH recommends that you contact your physician or local treatment centre. Before administering any […]

Medical sessions | WFH World Congress 2022

In these sessions from the WFH 2022 World Congress, David Lillicrap, Len Valentino, Sophie Susen, Mrinal Gounder, Rebecca Kruse-Jarres, Christine Mrakotsky, Roger Schutgens, Dan Hart, Margaret Rand, Karina Meijer Waander van Heerde, Keith Gomez, Emna Gouider, Charles Nakar, Brian R. Long, Tiago Lopes, Claire Pouplard, Radek Kaczmarek, Johnny Mahlangu, Steve Pipe, K. Rajender Reddy, Pratima […]

Questions to Ask Your Doctor Before Deciding to Take Gene Therapy

For people considering taking gene therapy, it is extremely important to learn as much as possible about if you are a good candidate, what the potential benefits and risks are, and what to expect during the procedure, and essential that your questions are answered. It may be helpful to write down a list of questions […]

WFH Gene Therapy Registry – User guide for people with hemophilia

This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR). It answers basic questions about the registry, its purpose, and what participants can expect. Please reach out to WFH with questions regarding participation in the registry at [email protected]. WFH Gene Therapy […]

WFH Gene Therapy Registry – User guide for hemophilia treatment centres

The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved in gene therapy. This includes HTCs that administer gene therapy and those that manage or follow-up with patients who have received gene therapy at other centres. This user guide will orient HTCs to the WFH […]