Year: 2025
Language: English
The WFH Guidelines for the Management of Hemophilia: AAV Gene Therapy provide the first comprehensive, evidence-based recommendations to support the safe, standardized, and effective implementation of AAV gene therapy in clinical practice. Developed by the WFH AAV Gene Therapy Panel, which is composed of gene therapy experts who were involved in clinical trials and healthcare teams currently treating patients who have received gene therapy, as well as people with hemophilia and their caregivers. These guidelines emphasize patient safety, informed decision-making, and long-term monitoring.
The WFH does not engage in the practice of medicine and under no circumstances recommends particular treatment for specific individuals. For diagnosis or consultation on a specific medical problem, the WFH recommends that you contact your physician or local treatment centre. Before administering any products, the WFH urges patients to check dosages with a physician or hemophilia centre staff, and to consult the pharmaceutical company’s printed instructions.
The WFH does not promote any particular pharmaceutical product and any mention of any commercial brand in this presentation is strictly for educational purposes.
This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH)
This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH)
The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved
The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved
This document is an introductory guide to the World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR). It answers basic
This document is an introductory guide to the World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR). It answers basic
