
Genetic Technologies for Hemophilia
Explore the science behind genetic technologies for hemophilia in this four-part video series from the WFH. Learn the basics of
Year: 2018
Language: English
Author(s): Spencer Sullivan
Format: Video
In the Tuesday morning session entitled Free Papers – Gene Therapy, Spencer Sullivan presents clinical results of FIX gene transfer using in vivo recombinant AAV delivery with the novel bioengineered vector SPA-9001, discussing vector design, FIX activity attained, and safety.

Explore the science behind genetic technologies for hemophilia in this four-part video series from the WFH. Learn the basics of

The WFH Guidelines for the Management of Hemophilia: AAV Gene Therapy provide the first comprehensive, evidence-based recommendations to support the

This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH)

This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH)

The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved

The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved