Year: 2018
Language: English
Author(s): Spencer Sullivan
In the Tuesday morning session entitled Free Papers – Gene Therapy, Spencer Sullivan presents clinical results of FIX gene transfer using in vivo recombinant AAV delivery with the novel bioengineered vector SPA-9001, discussing vector design, FIX activity attained, and safety.
This patient handbook contains basic information about gene therapy for hemophilia. The WFH does not engage in the practice of
In these sessions from the WFH 2022 World Congress, David Lillicrap, Len Valentino, Sophie Susen, Mrinal Gounder, Rebecca Kruse-Jarres, Christine
For people considering taking gene therapy, it is extremely important to learn as much as possible about if you are
This document is an introductory guide for people with hemophilia who wish to join the World Federation of Hemophilia (WFH)
The World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR) welcomes the participation of all Hemophilia Treatment Centres (HTCs) involved
This document is an introductory guide to the World Federation of Hemophilia (WFH) Gene Therapy Registry (GTR). It answers basic