Author(s): World Federation of Hemophilia
Date: June 18, 2020
We are still learning about gene therapy. Each patient experience is different, and gene therapy is not for everyone – either by choice or by exclusion because of the antibodies.
In this session from the WFH 2020 Virtual Summit, Debra Pollard, John Pasi, David Page, Garrett Hayes, Rob Schroeder and Enrique Preza Hernandez discuss: What can we expect if we ARE eligible – what is it like to participate in the gene therapy trials? What is it like to be a patient once you have gone through the treatment? What if it does not work for me (one and done) – can I try other future therapies?