Genomics of Platelet Disorders
In the Wednesday morning medical plenary session, Andrew Mumford presents an overview of the genomics of platelet disorders.
Hemophilia A Gene Therapy: AAV-mediated delivery of an enhanced F8 cassette to the liver produces supraphysiological levels of human FVIII in vivo
In the Tuesday morning session on gene therapy, Brigit E. Riley explains her approach to the AAV-mediated delivery of an enhanced F8 cDNA.