Achievement of Normal FVIII Activity Following Gene Transfer with Valoctocogene Roxaparvovec (BMN 270): Long-Term Efficacy and Safety Results in Patients with Severe Hemophilia A


Year: 2018

Language: English

Author(s): John Pasi

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In the Tuesday morning session entitled Free Papers – Gene Therapy, John Pasi presents results of the BMN 270-201 Phase 1/2 dose escalation hemophilia A clinical trial.