WFH NETWORK

Outcome Measures to Assess Curative Therapy

 
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Year: 2018

Language: English

Author(s): Alfonso Iorio

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In the Wednesday afternoon session entitled Past, Present, and Future of Gene Therapy: From Vectors and Transgenes to Outcomes, Alfonso Iorio discusses different efficacy and safety outcome measurements, particularly in the context of the coreHEM definition of the core outcome set for gene therapy in hemophilia.